{"id":361,"date":"2021-04-14T11:36:27","date_gmt":"2021-04-14T09:36:27","guid":{"rendered":"http:\/\/s804652872.mialojamiento.es\/wordpress\/projecte\/terapia-genica-per-curar-lataxia-de-friedreich\/"},"modified":"2021-05-14T16:06:00","modified_gmt":"2021-05-14T14:06:00","slug":"terapia-genica-para-curar-la-ataxia-de-friedreich","status":"publish","type":"projecte","link":"https:\/\/www.amicsdecanruti.org\/es\/projecte\/terapia-genica-para-curar-la-ataxia-de-friedreich\/","title":{"rendered":"Terapia g\u00e9nica para curar la Ataxia de Friedreich"},"content":{"rendered":"\n<p>Hemos desarrollado un tratamiento con un nuevo vector de terapia g\u00e9nica basado en virus adenoasociado (AAV) que administrado intratecalmente en una dosis \u00fanica en un modelo de rat\u00f3n con la ataxia de Friedreich cura los d\u00e9ficits neurol\u00f3gicos y card\u00edacos y previene la neurodegeneraci\u00f3n. Nuestro objetivo es continuar el desarrollo de este f\u00e1rmaco para implementar el tratamiento en pacientes con la enfermedad. Para ello primero necesitamos probar el f\u00e1rmaco de terapia g\u00e9nica en primates no humanos para comprobar que el f\u00e1rmaco es seguro, presenta una biodistribuci\u00f3n comparable a la que observamos en ratones y determinar la dosis efectiva.<\/p>\n","protected":false},"excerpt":{"rendered":"<p>Hemos desarrollado un tratamiento con un nuevo vector de terapia g\u00e9nica basado en virus adenoasociado (AAV) que administrado intratecalmente en [&hellip;]<\/p>\n","protected":false},"featured_media":0,"template":"","categories":[],"research_area":[261],"research_group":[296],"subject":[274],"institution":[13],"class_list":["post-361","projecte","type-projecte","status-publish","hentry","research_area-neurociencias","research_group-unidad-de-neurogenetica","subject-enfermedades-raras","institution-instituto-de-investigacion-germans-trias-i-pujol"],"acf":[],"_links":{"self":[{"href":"https:\/\/www.amicsdecanruti.org\/es\/wp-json\/wp\/v2\/projecte\/361","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/www.amicsdecanruti.org\/es\/wp-json\/wp\/v2\/projecte"}],"about":[{"href":"https:\/\/www.amicsdecanruti.org\/es\/wp-json\/wp\/v2\/types\/projecte"}],"wp:attachment":[{"href":"https:\/\/www.amicsdecanruti.org\/es\/wp-json\/wp\/v2\/media?parent=361"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/www.amicsdecanruti.org\/es\/wp-json\/wp\/v2\/categories?post=361"},{"taxonomy":"research_area","embeddable":true,"href":"https:\/\/www.amicsdecanruti.org\/es\/wp-json\/wp\/v2\/research_area?post=361"},{"taxonomy":"research_group","embeddable":true,"href":"https:\/\/www.amicsdecanruti.org\/es\/wp-json\/wp\/v2\/research_group?post=361"},{"taxonomy":"subject","embeddable":true,"href":"https:\/\/www.amicsdecanruti.org\/es\/wp-json\/wp\/v2\/subject?post=361"},{"taxonomy":"institution","embeddable":true,"href":"https:\/\/www.amicsdecanruti.org\/es\/wp-json\/wp\/v2\/institution?post=361"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}